With three FDA approvals in the past 10 months, there is a lot of momentum in the Duchenne muscular dystrophy space. Here are ...

Ohio Gov. Mike DeWine announced the state will be the first in the nation to screen newborns for the rare disease Duchenne ...

The drug-pricing watchdogs over at the Institute for Clinical and Economic Review tend to be supportive of gene therapy ...

The study provides evidence of survival benefits among patients with Duchenne muscular dystrophy (DMD) receiving eteplirsen ...

Ohio Gov. Mike DeWine on Monday announced that Ohio will become the first state in the nation to begin screening all newborn ...

Need a home remedy for your tooth infection? Try these expert-backed solutions to manage the discomfort while you wait to see ...

Columnist Betty Vertin has often grouped her three boys with DMD together, but she's recognizing their need for individual support.

Initiated dosing of the fourth and final cohort of Phase 1 clinical trial of ENTR-601-44 for the potential treatment of DMD with data readout on track for October of 2024 – – Achieved $75 million ...

A recent study suggests virtual reality and biofeedback training may be feasible and effective for patients with Duchenne ...

Ahead of the FDA’s June target action date for Sarepta’s Duchenne muscular dystrophy gene therapy, ICER Chief Medical Officer David Rind blasted the regulator’s accelerated pathway in a JAMA viewpoint ...

COLUMBUS — Ohio will become the first state to screen all newborn babies for Duchenne Muscular Dystrophy, a common hereditary ...

The mum of a child with a rare muscle wasting condition described as a “death sentence” says she wants to make every day count for her son.