The patients with myotonic dystrophy (hereafter also referred to as myotonics) did not differ significantly from the controls with Charcot-Marie-Tooth disease in terms of weakness or muscular atrophy.

Vertex Pharmaceuticals beat first quarter sales and earnings forecasts, but investors are closely watching its pipeline ...

The neurological examination showed percussion and grip myotonia, but no weakness, atrophy, or muscle hypertrophy. Widespread myotonic discharges and myopathic motor units were documented on EMG.

Calcium Channel Blockers Key to Reversing Myotonic Dystrophy Muscle Weakness Jan. 2, 2024 — New research has identified the specific biological mechanism behind the muscle dysfunction found in ...

Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today reported consolidated financial results for the first quarter ended ...

Fintel reports that on May 7, 2024, Piper Sandler upgraded their outlook for Design Therapeutics (NasdaqGS:DSGN) from Neutral ...

In a report released yesterday, Keay Nakae from Chardan Capital maintained a Buy rating on Dyne Therapeutics (DYN – Research Report), ...

As Republicans move forward with plans to vote on a farm bill, Democrats on the House Agriculture Committee have scheduled a meeting Thursday with House Minority Leader Hakeem Jeffries, D-N.Y., and ...

CARLSBAD, Calif., May 07, 2024 (GLOBE NEWSWIRE) -- (Nasdaq: DSGN), a biotechnology company developing treatments for serious degenerative genetic diseases, today announced that management will ...

Four days a week, twice per day, Martina Lemon carries her 34-pound, 4-year-old daughter Kierlyn in and out of the home to put her in a wheelchair and take her to and from school.It's a difficult ...

Patients with myotonic dystrophy have smaller hearts, and lower systolic and diastolic blood pressures and pulse rates. They have impaired autonomic reflexes, measured by orthostatic, Valsalva ...

Vertex announced that its U.S. Investigational New Drug Application (IND) for the Phase 1/2 clinical trial of VX-670 in people with myotonic dystrophy type 1 (DM1) has cleared, as have the Clinical ...