NHS, England
First Patient Begins Newly Approved Sickle Cell Gene Therapy
A 12-year-old boy in the Washington, D.C., area faces months of procedures to remedy his disease. “I want to be cured,” he said.
Opinion: A CRISPR breakthrough? The gene therapy has been approved to treat sickle-cell disease
A new gene therapy, utilizing the gene-editing tool known as CRISPR to treat sickle-cell disease, has received approval in the U.K., the U.S., and the EU. This milestone marks a potential breakthrough in alleviating the severe and life-threatening symptoms of sickle-cell disease while respecting ethical boundaries.
Black 12-Year-Old Patient Begins New Sickle Cell Therapy Treatment
A 12-year-old Black patient is the first to undergo a new gene therapy treatment for sickle cell disease, according to reports.
A 12-Year-Old Is First to Start New Sickle Cell Treatment
He's the first patient outside of a clinical trial to start a new genetic treatment that was shown in clinical trials to cure 88% of people of the hallmark symptoms of sickle cell disease.
World's first patient begins sickle cell gene therapy treatment: What is it?
Doctors in the US spent hours removing stem cells from the bone marrow of 12-year-old Kendric Cromer. These cells will be sent to a lab in New Jersey where researchers will infuse a healthy haemoglobin gene in them.
‘Life-changing’ sickle cell drug approved for NHS roll-out after patient-led campaign
Despite being the fastest-growing genetic condition in the UK, sickle cell disorder has historically been underserved by treatment options.
‘Life-changing’ drug for sickle cell disease to be offered by NHS in England
Voxelotor, which can help reduce need for blood transfusions, is administered as a daily tablet
NHS approves 'transformative' sickle cell treatment in England
Four thousand people diagnosed with sickle cell disease in England may now access "life-changing" treatment following its approval for NHS use. This treatment, known as voxelotor or oxbryta, and manufactured by Pfizer,
NHS to provide Pfizer’s Voxelotor to treat sickle cell disease
The NHS will immediately fund Voxelotor through the Innovative Medicines Fund, ensuring rapid access for patients. Clinical trials have demonstrated that Voxelotor could improve anaemia and reduce the necessity for repeated blood transfusions.
NHS approves 'life-changing' new sickle cell treatment for thousands of Brits
The drug, known as voxelotor, will be available immediately and could benefit around 4,000 people with sickle cell disease in England. It will significantly improve the quality of life for patients
How a new NHS treatment for sickle cell disease could offer patients some hope
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