I’ve written a lot about the support I’ve received from nurses and others. Although I always recognize the people in my life ...
Evrysdi and discontinued drug branaplam have a similar mechanism, but Evrysdi has more specific target in genetic code, SMA ...
A swallowing technique with effort called vacuum swallowing helped ease problems with swallowing for a man, 67, with spinal ...
Implementing the global compassionate use program for Evrysdi for SMA required careful considerations of local regulations, ...
Without treatment, most people with spinal muscular atrophy (SMA) who have four copies of the “backup” SMN2 gene will start ...
When columnist Sherry Toh realizes some of her behaviors could actually be symptoms, she explores the possibility that she ...
That’s the text my caregiver, Christian, sent me several months ago when he found out that “Star Wars” actor Hayden ...
Jasmine Ramos is a junior at Millersville University of Pennsylvania. As a student involvement assistant at her community college, she’s managed the school newsletter, earning her the affectionate ...
Our online provider finder is designed to help spinal muscular atrophy (SMA) patients and caregivers find a specialist near them. Enter your information below to locate healthcare providers in your ...
Peeking up from my pillow and seeing that it was 4:55 a.m. was an unpleasant surprise the other day. I had slept only a whopping 20 minutes longer than the night before, and it was becoming a pattern.
Scholar Rock remains on track to report topline results later this year from its ongoing Phase 3 clinical trial of apitegromab in children and young adults with spinal muscular atrophy (SMA) types 2 ...