A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new ...

Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after ...

A research team has developed and safely delivered a personalized gene editing therapy to treat ... six months and marks the first time the technology has been successfully deployed to treat ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ... among the first to be successfully treated with a custom therapy ...

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

PHILADELPHIA — A baby ... gene editing treatment made just for him. Researchers described the case in a new study, saying he’s among the first to be successfully treated with a custom therapy ...

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

Personalized CRISPR treatment used on baby with genetic disease by Steph Whiteside - 05/15/25 4:15 PM ET The baby's disease prevented the liver from removing ammonia ...

In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to successfully receive a personalized CRISPR gene editing therapy. The ...

A research team supported by the National Institutes of Health (NIH) has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable ...

They corrected a specific gene mutation in the baby’s liver cells that led to the disorder. CRISPR is an advanced gene editing technology that enables precise changes to DNA inside living cells. This ...